Capabilities
Core capabilities and outputs
Practical deliverables for teams preparing construct designs, CRO-facing studies, diligence reviews, or ongoing preclinical execution.
1
DNA construct design
For companies needing plasmids, AAV/LVV constructs, promoter/enhancer designs, reporters, barcodes, or expression cassettes.
- Construct architecture recommendation
- Annotated DNA maps
- Sequence design review
- Codon/regulatory element review
- Cloning/vendor-ready design package
- Risk assessment: repeats, recombination, cryptic splicing, CpG, payload limits, LTR and ITR
2
CRO-ready study design
For teams preparing in vitro, in vivo, biodistribution, expression, potency, or exploratory pharmacology studies.
- Study objective and decision gate
- Experimental design
- Arms, controls, endpoints, and sample size logic
- Materials list
- Data package expectations
3
CRO selection and management
For small teams that know what they need but cannot manage execution.
- CRO shortlist
- Quote comparison
- Technical evaluation
- Kickoff meeting
- Weekly oversight
- Data review, deviation management, and final report review
4
Gene therapy technical diligence
For investors, company founders, or BD teams evaluating an asset.
- Vector/design review
- Preclinical package analysis
- Manufacturability risks
- Translational risks
- Competitive landscape
- Key risks and recommended next experiments
5
Fractional scientific lead
For seed-stage companies without a full-time head of platform/preclinical.
- Standing weekly advisory
- Study planning
- Vendor oversight
- Technical slide review
- Founder/investor support
- Internal program strategy
6
AI / Data / Bioinformatics
Additional capability for evidence generation, prioritization, and data-analysis workflows.
- Promoter/enhancer discovery and prioritization
- Construct risk screen
- Literature and competitive landscape synthesis
- Target expression evidence package
- Cross-species conservation review
- Single-cell/ATAC/RNA-seq workflow design and analysis support